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aav-gene-editors

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Validated AAV vector designs for in vivo CRISPR gene editing. Includes hfCas12Max, SaCas9, and CasMINI with customizable promoters and guide RNAs optimized for AAV packaging constraints.

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Ambryon/aav-gene-editors · Validated AAV vector designs for in vivo CRISPR gene editing. Includes hfCas12Max, SaCas9, and CasMINI with customizable promoters and guide RNAs optimized for AAV packaging constraints.